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Updated: Sep 5, 2025

Modeling Myotonic Dystrophy 1 in C2C12 Myoblast Cells
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Selective and Reversible Ligand Assembly on the DNA and RNA Repeat Sequences in Myotonic Dystrophy

Sarah B Krueger1, Amie N Lanzendorf1, Hyoeun Heather Jeon1

  • 1Department of Chemistry, University of Illinois at Urbana-Champaign, 600 S Mathews Ave, Urbana, IL 61801, USA.

Chembiochem : a European Journal of Chemical Biology
|July 5, 2022
PubMed

Keywords:
drug designmyotonic dystrophy type 1nucleic acidssmall moleculestranscription inhibition

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