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Editorial: Lessons Learned from Translational Research in Neuromuscular Diseases: Impact on Study Design, Outcome

Anna G Mayhew1, Leslie Nelson2, Michela Guglieri1

  • 1The John Walton Muscular Dystrophy Research Centre, Translational and Clinical Research Institute, Newcastle University and Newcastle Hospitals NHS Foundation Trust, Newcastle upon Tyne, United Kingdom.

Frontiers in Genetics
|July 21, 2022
PubMed
Abstract

No abstract available in PubMed .

Keywords:
clinical outcome assessmentsclinical trialduchenne muscular dystrophy (DMD)neuromuscular disorders (NMD)remote assessmentspinal muscular atrophy (SMA)

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