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Current Strategies of Muscular Dystrophy Therapeutics: An Overview

Kenji Rowel Q Lim1, Toshifumi Yokota2,3

  • 1Department of Medical Genetics, Faculty of Medicine and Dentistry, University of Alberta, Edmonton, AB, Canada.

Methods in Molecular Biology (Clifton, N.J.)
|November 18, 2022
PubMed

Keywords:
Antisense oligonucleotidesCRISPRCell therapyGene replacementMuscular dystrophyNonsense suppressionSmall molecule compounds

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