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Editorial: The use of real world data for regulatory purposes in the rare diseases setting

Viviana Giannuzzi1, Violeta Stoyanova-Beninska2, Virginie Hivert3

  • 1Research Department, Fondazione per la Ricerca Farmacologica Gianni Benzi Onlus, Valenzano, Italy.

Frontiers in Pharmacology
|December 12, 2022
PubMed
Abstract

No abstract available in PubMed .

Keywords:
medicine regulationorphan medicinesrare diseasesreal world datareal world evidence

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