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Editorial: Viral vector-based gene therapy in neurological disease: The future is now

Jared B Smith1, Laura Cancedda2, Sergiusz Jozwiak3

  • 1Research and Early Development, REGENXBIO Inc., Rockville, MD, United States.

Frontiers in Neurology
|March 3, 2023
PubMed
Abstract

No abstract available in PubMed .

Keywords:
adeno-associated virus (AAV)antibodygene replacementgene therapypromoterspinal muscular atrophy (SMA)viral vector

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