Synthesis and Preclinical Evaluation of a Novel FAPI-04 Dimer for Cancer Theranostics

Xuan Zhong1,2, Jingru Guo3, Xiuping Han4

  • 1Nanjing University of Chinese Medicine, Nanjing 210046, China.

Insights

A novel dimeric fibroblast activation protein inhibitor (FAPI) derivative, DOTA-Suc-Lys-(FAPI-04)2, enhances tumor uptake and retention for improved nuclear imaging and radionuclide therapy. This FAPI dimer shows significant potential in cancer theranostics.

Area of Science:

  • Nuclear Medicine
  • Oncology
  • Radiochemistry

Background:

  • Fibroblast activation protein (FAP) is overexpressed in cancer-associated fibroblasts across various tumors, making it a selective target.
  • FAP inhibitors (FAPIs) labeled with radionuclides are used for tumor imaging, but their short retention limits therapeutic applications.
  • Developing FAPIs with improved tumor retention is crucial for effective radionuclide therapy.

Purpose of the Study:

  • To synthesize and evaluate a novel dimeric FAPI derivative (DOTA-Suc-Lys-(FAPI-04)2) for enhanced tumor targeting, imaging, and radionuclide therapy.
  • To investigate the biodistribution, retention, and efficacy of radiolabeled FAPI dimer in preclinical cancer models.
  • To assess the potential of the FAPI dimer for improved tumor theranostics.

Main Methods:

  • Synthesis of the DOTA-Suc-Lys-(FAPI-04)2 complex using Fmoc-Lys(Boc)-OH as a linker.
  • Radiolabeling of the dimer with Gallium-68 ([68Ga]) for imaging and Lutetium-177 ([177Lu]) for therapy.
  • In vitro stability assessment and in vivo micro-PET imaging in SKOV3, A431, and H1299 xenografts.
  • Evaluation of antitumor efficacy and tolerance of [177Lu]Lu-(FAPI-04)2 in tumor-bearing models.

Main Results:

  • The radiolabeled FAPI dimer ([68Ga]Ga-(FAPI-04)2) demonstrated >99% radiochemical purity and in vitro stability.
  • In vivo studies showed approximately twofold higher tumor uptake and prolonged retention of [68Ga]Ga-(FAPI-04)2 compared to the monomeric FAPI.
  • The FAPI dimer achieved significantly higher tumor-to-background ratios than [18F]F-FDG.
  • [177Lu]Lu-(FAPI-04)2 effectively inhibited tumor growth with good tolerance.

Conclusions:

  • The DOTA-Suc-Lys-(FAPI-04)2 design significantly enhances FAP-targeting efficacy, improving tumor uptake and retention.
  • Radiolabeled FAPI dimer enables high-contrast imaging and demonstrates a notable antitumor effect, supporting its theranostic potential.
  • This novel dimeric FAPI derivative offers a promising strategy for advancing FAPI-based tumor theranostics.

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