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Published on: June 2, 2023
Current perspectives on the management of patients with advanced RET-driven thyroid cancer in Europe
Rossella Elisei1, Enrique Grande2, Michael C Kreissl3
1Endocrine Unit, Department of Clinical and Experimental Medicine, University of Pisa, Pisa, Italy.
Abstract:
The incidence of thyroid cancer is increasing worldwide with the disease burden in Europe second only to that in Asia. In the last several decades, molecular pathways central to the pathogenesis of thyroid cancer have revealed a spectrum of targetable kinases/kinase receptors and oncogenic drivers characteristic of each histologic subtype, such as differentiated thyroid cancer, including papillary, follicular, and medullary thyroid cancer. Oncogenic alterations identified include B-Raf proto-oncogene (BRAF) fusions and mutations, neurotrophic tyrosine receptor kinase (NTRK) gene fusions, and rearranged during transfection (RET) receptor tyrosine kinase fusion and mutations. Multikinase inhibitors (MKIs) targeting RET in addition to multiple other kinases, such as sorafenib, lenvatinib and cabozantinib, have shown favourable activity in advanced radioiodine-refractory differentiated thyroid cancer or RET-altered medullary thyroid cancer; however, the clinical utility of MKI RET inhibition is limited by off-target toxicity resulting in high rates of dose reduction and drug discontinuation. Newer and selective RET inhibitors, selpercatinib and pralsetinib, have demonstrated potent efficacy and favourable toxicity profiles in clinical trials in the treatment of RET-driven advanced thyroid cancer and are now a therapeutic option in some clinical settings. Importantly, the optimal benefits of available specific targeted treatments for advanced RET-driven thyroid cancer require genetic testing. Prior to the initiation of systemic therapy, and in treatment-naïve patients, RET inhibitors may be offered as first-line therapy if a RET alteration is found, supported by a multidisciplinary team approach.
Insights
Newer targeted therapies, including selective rearranged during transfection (RET) inhibitors, show promise for advanced thyroid cancer. Genetic testing is crucial for identifying RET alterations to guide optimal, personalized treatment strategies.
Area of Science:
- Oncology
- Molecular Biology
- Pharmacology
Background:
- Thyroid cancer incidence is rising globally, with significant disease burden in Europe.
- Molecular pathways reveal targetable oncogenic drivers like BRAF, NTRK, and RET in various thyroid cancer subtypes.
- Multikinase inhibitors (MKIs) targeting RET have shown activity but are limited by toxicity.
Purpose of the Study:
- To review the evolving landscape of targeted therapies for advanced thyroid cancer.
- To highlight the efficacy and safety of newer, selective RET inhibitors.
- To emphasize the importance of genetic testing for identifying RET alterations.
Main Methods:
- Review of current literature on thyroid cancer pathogenesis and targeted therapies.
- Analysis of clinical trial data for multikinase inhibitors and selective RET inhibitors.
- Discussion of treatment guidelines and the role of genetic testing.
Main Results:
- Selective RET inhibitors (selpercatinib, pralsetinib) demonstrate potent efficacy and improved toxicity profiles compared to MKIs.
- RET alterations are key drivers in specific thyroid cancer subtypes, including medullary and differentiated thyroid cancer.
- Genetic testing is essential for identifying patients who will benefit from RET-targeted therapies.
Conclusions:
- Selective RET inhibitors represent a significant advancement in treating advanced RET-driven thyroid cancer.
- Personalized treatment approaches based on genetic testing are crucial for optimizing patient outcomes.
- Multidisciplinary team involvement is recommended for effective management of these complex cases.

