Related Experiment Video
Updated: Jun 14, 2026

09:21
Production, Purification, and Quality Control for Adeno-associated Virus-based Vectors
Published on: January 29, 2019
36.6K
Molecular evaluation and vector integration analysis of HCC complicating AAV gene therapy for hemophilia B
Manfred Schmidt1, Graham R Foster2, Michiel Coppens3,4
1GeneWerk GmbH, Heidelberg, Germany.
Blood Advances
|June 23, 2023
Abstract
No abstract available in PubMed .
More Related Videos
09:20Isolation of Next-Generation Gene Therapy Vectors through Engineering, Barcoding, and Screening of Adeno-Associated Virus AAV Capsid Variants
Published on: October 18, 2022
4.6K
04:43Author Spotlight: Optimizing Digital Droplet PCR Method for Accurate Adeno-Associated Viral Genome Quantification
Published on: October 11, 2024
2.0K
Related Concept Videos
Gene Therapy
Gene therapy is a technique where a gene is inserted into a person’s cells to prevent or treat a serious disease. The added gene may be a healthy version of the gene that is mutated in the patient, or it could be a different gene that inactivates or compensates for the patient’s disease-causing gene. For example, in patients with severe combined immunodeficiency (SCID) due to a mutation in the gene for the enzyme adenosine deaminase, a functioning version of the gene can be inserted. The...
Gene Therapy
Gene therapy is a technique where a gene is inserted into a person’s cells to prevent or treat a serious disease. The added gene may be a healthy version of the gene that is mutated in the patient, or it could be a different gene that inactivates or compensates for the patient’s disease-causing gene. For example, in patients with severe combined immunodeficiency (SCID) due to a mutation in the gene for the enzyme adenosine deaminase, a functioning version of the gene can be inserted. The...