Isolation and characterization of β-transducin repeat-containing protein ligands screened using a high-throughput

Xintong Liu1,2,3, Emiko Sanada1,3,4, Jiang Li5

  • 1Chemical Resource Development Research Unit, RIKEN CSRS, Wako, Saitama, 351-0198, Japan.

Oncology Research
|August 7, 2023
PubMed

Insights

Researchers developed a high-throughput screening system to identify small molecule ligands for β-transducin repeat-containing protein (β-TrCP). Several compounds were found to inhibit β-TrCP activity in cells, impacting NF-κB signaling.

Area of Science:

  • Biochemistry and Molecular Biology
  • Drug Discovery and Development

Background:

  • β-transducin repeat-containing protein (β-TrCP) is a crucial component of the SCF E3 ubiquitin ligase complex, dictating substrate specificity.
  • Targeting β-TrCP is of interest for developing novel therapeutic strategies, including proteolysis targeting chimeras (PROTACs).

Purpose of the Study:

  • To develop a high-throughput screening (HTS) system for identifying small molecule ligands of β-TrCP.
  • To discover potent β-TrCP ligands for potential future application in PROTAC technology.
  • To investigate the mechanism of action and key structural features of identified β-TrCP inhibitors.

Main Methods:

  • Development and implementation of an HTS system to screen a chemical library for β-TrCP ligands.
  • In vitro assessment of hit compounds' effects on SCFβ-TrCP1 ubiquitination activity.
  • Evaluation of hit compounds' impact on TNFα-induced IκBα degradation and NF-κB transcriptional activity in cells.
  • In silico analysis to identify key functional groups responsible for β-TrCP binding.

Main Results:

  • Several hit compounds, including NPD5943, NPL62020-01, and NPL42040-01, were identified.
  • These compounds effectively inhibited the TNFα-induced degradation of IκBα and its phosphorylated form, thereby suppressing NF-κB activation.
  • In silico analysis revealed that carboxyl and hydroxyl groups in the hit compounds form hydrogen bonds with β-TrCP, mimicking interactions with natural phosphopeptide substrates.

Conclusions:

  • The study successfully established an HTS system for discovering β-TrCP ligands.
  • Identified small molecules demonstrate potent inhibition of β-TrCP activity in cellular contexts.
  • The findings provide valuable insights into the structural requirements for β-TrCP ligand design, crucial for PROTAC development.