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First regulatory qualification of a digital primary endpoint to measure treatment efficacy in DMD

Laurent Servais1,2, Damien Eggenspieler3, Margaux Poleur4

  • 1Department of Paediatrics, MDUK Oxford Neuromuscular Centre & NIHR Oxford Biomedical Research Centre, University of Oxford, Oxford, UK. laurent.servais@paediatrics.ox.ac.uk.

Nature Medicine
|October 9, 2023
PubMed
Abstract

No abstract available in PubMed .

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