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Nusinersen for Spinal Muscular Atrophy Type I with Chronic Respiratory Failure: A Retrospective Study in South Korea

Hui Jin Shin1, Ji-Hoon Na1, Hyunjoo Lee1

  • 1Department of Pediatrics, Gangnam Severance Hospital, Severance Children's Hospital, Yonsei University College of Medicine, Seoul, Korea.

Yonsei Medical Journal
|November 22, 2023
PubMed
Abstract

Keywords:
South KoreaSpinal muscular atrophymotor functionnusinersenrespiratory failure

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