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First successful outcomes of pegvaliase (PALYNZIQ) in children

Majid Alfadhel1,2,3, Rayyan Albarakati4

  • 1College of Medicine, King Saud bin Abdulaziz University for Health Sciences (KSAU-HS), King Abdulaziz Medical City, Ministry of National Guard Health Affairs (MNG-HA), Riyadh, Saudi Arabia. dralfadhelm@gmail.com.

BMC Medical Genomics
|March 22, 2024
PubMed
Abstract

Keywords:
Case ReportPALYNZIQ®PediatricPegvaliasePhenylalanine hydroxylase, PAH, PKUPhenylketonuria

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