Rolapitant treats lung cancer by targeting deubiquitinase OTUD3

Tongde Du1, Quan Gu1, Yonghui Zhang2

  • 1Jiangsu Cancer Hospital, Jiangsu Institute of Cancer Research, The Affiliated Cancer Hospital of Nanjing Medical University, Nanjing, 210009, Jiangsu, China.

Abstract

Insights

Rolapitant inhibits deubiquitinase OTUD3, a key factor in lung cancer progression. This drug promotes cancer cell death by targeting the OTUD3-GRP78 axis and upregulating death receptor 5, offering a new therapeutic strategy.

Area of Science:

  • Oncology
  • Molecular Biology
  • Drug Discovery

Background:

  • Lung cancer remains a leading cause of global mortality, necessitating novel therapeutic interventions.
  • Targeting the ubiquitin-proteasome system with small molecule inhibitors, particularly deubiquitinase inhibitors, shows promise for cancer treatment.
  • The deubiquitylase OTUD3 promotes lung tumorigenesis by stabilizing oncoprotein GRP78, suggesting OTUD3 inhibition as a potential lung cancer therapy.

Purpose of the Study:

  • To identify a small molecule inhibitor of OTUD3 from FDA-approved drugs.
  • To investigate the therapeutic potential of OTUD3 inhibition in lung cancer.
  • To elucidate the molecular mechanisms by which OTUD3 inhibition affects lung cancer cells.

Main Methods:

  • Computer-aided virtual screening and experimental validation were used to identify OTUD3 inhibitors.
  • Quantitative proteomic profiling was employed to analyze drug-induced molecular changes.
  • In vitro cell proliferation and apoptosis assays, along with in vivo xenograft studies, were conducted.

Main Results:

  • Rolapitant was identified as a novel small molecule inhibitor of OTUD3, suppressing lung cancer cell proliferation.
  • Rolapitant upregulated death receptor 5 (DR5) expression, enhancing TRAIL-induced apoptosis.
  • The drug triggered endoplasmic reticulum (ER) stress and CHOP-DR5 signaling via the OTUD3-GRP78 axis, sensitizing cells to apoptosis.
  • In vivo, Rolapitant effectively suppressed lung cancer xenograft growth without significant toxicity.

Conclusions:

  • Rolapitant is a novel inhibitor of the deubiquitinase OTUD3.
  • The OTUD3-GRP78 axis represents a viable therapeutic target for lung cancer treatment.
  • Rolapitant demonstrates potential as an anti-lung cancer drug by inducing apoptosis through ER stress and DR5 upregulation.