Novel biallelic ZNF335 variant causing primary microcephaly: A case report and radiological review

Dhrumil Deveshkumar Patel1, Karen W Gripp2, Erin Wadman2

  • 1Department of Radiology, Nemours Children's Health, Wilmington, Delaware, USA.

Insights

Genetic variants in ZNF335 cause microcephaly by affecting neural development. This study identifies a novel ZNF335 variant linked to primary microcephaly and brain abnormalities in a Nepalese patient.

Area of Science:

  • Genetics
  • Neuroscience
  • Developmental Biology

Background:

  • Biallelic pathogenic variants in ZNF335 are a recently identified genetic cause of microcephaly.
  • ZNF335 plays a crucial role in regulating neural progenitor proliferation and neurogenesis via interaction with a H3K4 methyltransferase complex.
  • Pathogenic ZNF335 variants can lead to neuronal cell death and aberrant differentiation, resulting in secondary microcephaly.

Observation:

  • A novel homozygous ZNF335 splice site variant (c.3591+2dup) was identified in an individual of Nepalese ancestry.
  • The patient presented with primary microcephaly, characterized by atrophic cerebral hemispheres, simplified gyri, basal ganglia abnormalities, and corpus callosal atrophy.
  • RNA analysis confirmed the variant as a splice site mutation in intron 23.

Findings:

  • The identified ZNF335 variant contributes to primary microcephaly and significant neurodevelopmental anomalies.
  • The patient's phenotype includes severe brain abnormalities affecting the cortex, posterior fossa, and basal ganglia.
  • This case expands the known spectrum of ZNF335-associated microcephaly.

Implications:

  • Understanding ZNF335's role in neurodevelopment is critical for diagnosing and potentially treating microcephaly.
  • Identification of novel variants like the one reported here refines genotype-phenotype correlations in ZNF335-related disorders.
  • Further research into ZNF335 function may reveal therapeutic targets for neurodevelopmental disorders.