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Promise of gene therapy for congenital neurologic disease due to GPI deficiency

Daria V Babushok1,2, Denise E Sabatino3,4

  • 1Division of Hematology-Oncology, Department of Medicine, University of Pennsylvania, 3400 Civic Center Boulevard, Philadelphia, PA 19104, USA.

Molecular Therapy. Methods & Clinical Development
|April 4, 2024
PubMed
Abstract

No abstract available in PubMed .

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