Related Experiment Video

Updated: Jun 28, 2025

Adeno-Associated Virus-Mediated Delivery of CRISPR for Cardiac Gene Editing in Mice
09:00

Adeno-Associated Virus-Mediated Delivery of CRISPR for Cardiac Gene Editing in Mice

Published on: August 2, 2018

8.2K

FDA approves an HDAC inhibitor for Duchenne muscular dystrophy

Asher Mullard

    Nature Reviews. Drug Discovery
    |April 11, 2024
    PubMed
    Abstract

    No abstract available in PubMed .

    More Related Videos

    Characterizing Exon Skipping Efficiency in DMD Patient Samples in Clinical Trials of Antisense Oligonucleotides05:16

    Characterizing Exon Skipping Efficiency in DMD Patient Samples in Clinical Trials of Antisense Oligonucleotides

    Published on: May 7, 2020

    6.8K
    Exon Skipping in Directly Reprogrammed Myotubes Obtained from Human Urine-Derived Cells06:20

    Exon Skipping in Directly Reprogrammed Myotubes Obtained from Human Urine-Derived Cells

    Published on: May 7, 2020

    7.1K

    Related Concept Videos

    Satellite Stem Cells and Muscular Dystrophy01:21

    Satellite Stem Cells and Muscular Dystrophy

    Satellite stem cells or myosatellite cells are quiescent stem cells that Alexander Mauro first identified in 1961. These cells are located between the sarcolemma, the plasma membrane of muscle fibers, and the basal lamina, the connective tissue sheath covering it. These mononucleated cells are activated in response to muscle injury, can transform into myoblasts, and may form or repair muscle fibers. Myosatellite cells can provide additional myonuclei for muscle regeneration or return to a...
    2.0K