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AAV vectors for long-term gene therapy of hemophilia B: Are we there yet?

Arun Srivastava1

  • 1Division of Cellular and Molecular Therapy, Departments of Pediatrics and Molecular Genetics & Microbiology, Powell Gene Therapy Center, Cancer and Genetics Research Complex, University of Florida College of Medicine, 2033 Mowry Road, Gainesville, FL 32611, USA.

Molecular Therapy : the Journal of the American Society of Gene Therapy
|June 21, 2024
PubMed
Abstract

No abstract available in PubMed .

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