Undetected Neuromuscular Disease in Patients after Heart Transplantation

Biniam Melese Bekele1,2,3,4, Elisabetta Gazzerro1,2, Felix Schoenrath3,4,5

  • 1Muscle Research Unit, ECRC Experimental and Clinical Research Center, Charité-Universitätsmedizin Berlin, corporate member of Freie Universität Berlin and Humboldt-Universität zu Berlin, Lindenberger Weg 80, 13125 Berlin, Germany.

Insights

Heart transplantation (HTX) generally preserves skeletal muscle function, but some patients develop myopathy due to genetic causes. Genetic testing and neurological assessments are recommended during the HTX period.

Area of Science:

  • Cardiology
  • Neurology
  • Genetics

Background:

  • Heart transplantation (HTX) is a treatment for end-stage heart failure patients with cardiomyopathies (CMPs).
  • Genetic factors underlie most CMPs, with known overlap between cardiac and skeletal myopathies.
  • Long-term skeletal muscle function and potential undiagnosed genetic causes post-HTX remain unclear.

Purpose of the Study:

  • To evaluate long-term skeletal muscle function in heart transplant recipients.
  • To identify potential undiagnosed genetic causes of cardiac and skeletal pathologies.

Main Methods:

  • Thirty-nine HTX patients underwent interviews on muscle function, quality-of-life surveys (EuroQol EQ-5D-3L), and physical examinations (MRC Muscle scale).
  • Whole-exome sequencing was performed on patients with skeletal muscle weakness.

Main Results:

  • 17.9% of patients reported new-onset muscle weakness and motor limitations.
  • Four patients exhibited objective muscle weakness; three had pathogenic variants identified (nexilin, myosin heavy chain, titin, SPG7 genes).
  • Approximately 10% of patients showed clinical signs of genetic myopathy.

Conclusions:

  • Skeletal muscle function generally has a positive long-term outcome post-HTX.
  • A subset of HTX patients may have undiagnosed genetic myopathies.
  • Integrating genetic testing and neurological assessments during the peri-HTX period is advisable.

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