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In vivo genome editing for inherited retinal disease: Opportunities and challenges

Rob W J Collin1, Bart P Leroy2

  • 1Department of Human Genetics, Radboud Institute for Medical Innovation, Radboud University Medical Center, Nijmegen, the Netherlands.

Molecular Therapy : the Journal of the American Society of Gene Therapy
|July 31, 2024
PubMed
Abstract

No abstract available in PubMed .

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