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Stereopure ASOs: An unanticipated increase in selectivity for targeting mutant HTT

Vijay N Gulumkar1, Steven F Dowdy1

  • 1Department of Cellular & Molecular Medicine, University of California, San Diego, School of Medicine, La Jolla, CA, USA.

Molecular Therapy. Nucleic Acids
|September 16, 2024
PubMed
Summary

No abstract available in PubMed .

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