Progressive Polycystic Kidney Disease in an Infant Girl With TSC2/PKD1 Contiguous Gene Syndrome

Kazuhiko Hashimoto1, Takuya Hayashida1, Yoshikazu Otsubo1

  • 1Department of Pediatrics, Sasebo City General Hospital, Sasebo, JPN.

Cureus
|September 26, 2024
PubMed

Insights

TSC2/PKD1 contiguous gene syndrome, a rare genetic disorder, causes severe kidney cysts and enlargement. Early genetic testing and frequent imaging are crucial for managing this condition and preventing hypertension.

Area of Science:

  • Genetics
  • Pediatric Nephrology
  • Medical Imaging

Background:

  • TSC2/PKD1 contiguous gene syndrome results from deletions in TSC2 and PKD1 genes.
  • This syndrome leads to tuberous sclerosis complex and autosomal dominant polycystic kidney disease.
  • Characterized by early-onset severe cystic kidney disease with progressive kidney and cyst enlargement.

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