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Allele-specific CRISPR-Cas9 editing inactivates a single-nucleotide variant associated with collagen VI muscular

Yoshitsugu Aoki1

  • 1Department of Molecular Therapy, National Institute of Neuroscience, National Center of Neurology and Psychiatry (NCNP), Tokyo, Japan.

Molecular Therapy. Nucleic Acids
|October 9, 2024
PubMed
Abstract

No abstract available in PubMed .

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