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Weighing the Risks of Lentiviral Gene Therapy for Cerebral Adrenoleukodystrophy

Cynthia E Dunbar1

  • 1From the Translational Stem Cell Biology Branch, National Heart, Lung, and Blood Institute, National Institutes of Health, Bethesda, Maryland.

The New England Journal of Medicine
|October 9, 2024
PubMed
Abstract

No abstract available in PubMed .

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