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Gene therapy trial lights the way for patients with Leber congenital amaurosis 1

Ying Kai Chan1

  • 1Cirrus Therapeutics, Cambridge, MA, USA; Academic Unit of Ophthalmology, Translational Health Sciences, University of Bristol, BS8 1TD Bristol, UK.

Molecular Therapy : the Journal of the American Society of Gene Therapy
|October 26, 2024
PubMed
Abstract

No abstract available in PubMed .

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