Phase Ib study of the oral PI3Kδ inhibitor linperlisib in patients with advanced solid tumors

Jin Li1, Junli Xue2, Tianshu Liu3

  • 1Department of Oncology, East Hospital Affiliated to Tongji University, No. 150 Jimo Road, Pudong New Area, Shanghai, 200120, China. jili9871116@163.com.

Abstract

Insights

Linperlisib, a PI3Kδ inhibitor, demonstrated an acceptable safety profile and preliminary clinical benefit in patients with advanced solid tumors. Further investigation into its safety and efficacy is warranted.

Area of Science:

  • Oncology
  • Pharmacology
  • Clinical Trials

Background:

  • Patients with advanced solid tumors face poor prognoses.
  • Investigating novel targeted therapies is crucial for improving outcomes.
  • Linperlisib, a selective PI3Kδ inhibitor, is explored for its potential in this patient population.

Purpose of the Study:

  • To assess the safety and feasibility of linperlisib in patients with advanced solid tumors.
  • To evaluate the preliminary clinical activity of linperlisib.

Main Methods:

  • A phase Ib, single-arm, open-label, multi-center clinical trial was conducted.
  • 94 patients with advanced solid tumors received oral linperlisib (80 mg/day).
  • The primary endpoint was safety assessment, with secondary endpoints including efficacy measures.

Main Results:

  • The most frequent treatment-emergent adverse events included elevated liver enzymes and proteinuria.
  • Grade ≥3 adverse events of special interest included diarrhea and cytopenias.
  • The objective response rate was 1.1%, and the disease control rate was 37.2% with a median PFS of 1.85 months.

Conclusions:

  • Linperlisib exhibited an acceptable safety profile in patients with advanced solid tumors.
  • Preliminary clinical benefit was observed, suggesting potential therapeutic value.
  • Further studies are recommended to confirm the safety and efficacy of linperlisib.