Nucleic acid drugs: recent progress and future perspectives.

Xiaoyi Sun1, Sarra Setrerrahmane2, Chencheng Li1

  • 1Jiangsu Province Engineering Research Center of Synthetic Peptide Drug Discovery and Evaluation, China Pharmaceutical University, Nanjing, 210009, China.

Summary

Nucleic acid drugs (NADs) offer efficient gene editing but face delivery challenges. Advances in chemical modification and delivery strategies are improving their stability, targeting, and clinical application for various diseases.

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