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Case Report: A Novel Homozygous Variant of the CTSK Gene in Rare Pycnodysostosis
Irina Zhargalovna Zhalsanova1, Elizaveta Alekseevna Fonova1, Nail Raushanovich Valiakhmetov1
1Research Institute of Medical Genetics, Tomsk National Research Medical Center, Tomsk 634050, Russia.
Abstract:
Pycnodysostosis (PD) is a rare autosomal recessive skeletal dysplasia from impaired bone resorption due to osteoclastic dysfunction. The features of PD are deformity of the skull, maxilla, and phalanges; osteosclerosis; and bone fragility. We describe the case of a patient with complaints of multiple fractures of the lower extremities in the anamnesis and pain in the lower extremities, cervical spine, and shoulder girdle during physical exertion. Genetic testing revealed a novel homozygous variant c.704T>C (p.Leu235Pro) in the CTSK gene. Biallelic pathogenic variants in this gene lead to PD. Thus, the diagnosis in the patient was established by finding a novel likely pathogenic variant in the CTSK gene.
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