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Updated: Jun 4, 2025

A Precision Medicine Tool for Measurement and Monitoring of Hemoglobin S in Sickle Cell Disease Patients Receiving Transfusion Therapy
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Sickle cell anaemia therapy in 2025

Alan N Schechter1

  • 1Molecular Medicine Branch, National Institute of Diabetes and Digestive and Kidney Diseases, National Institutes of Health, Bethesda, Maryland, USA.

British Journal of Haematology
|December 23, 2024
PubMed
Summary

New sickle cell anaemia treatments show limited success. This review questions if hydroxyurea, a current therapy, deserves more focus given the slow progress of stem cell and gene therapies.

Keywords:
fetal haemoglobinhydroxyureasickle cell anaemiatherapy

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