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Advanced In Vitro Models for Preclinical Drug Safety: Recent Progress and Prospects
Dileep G Nair1,2, Ralf Weiskirchen1
1Institute of Molecular Pathobiochemistry, Experimental Gene Therapy and Clinical Chemistry (IFMPEGKC), University Hospital Aachen, D-52074 Aachen, Germany.
Abstract:
The majority of drugs are typically orally administered. The journey from drug discovery to approval is often long and expensive, involving multiple stages. A major challenge in the drug development process is drug-induced liver injury (DILI), a condition that affects the liver, the organ responsible for metabolizing most drugs. Traditionally, identifying DILI risk has been difficult due to the poor correlation between preclinical animal models and in vitro systems. Differences in physiology between humans and animals or cell lines contribute to the failure of many drug programs during clinical trials. The use of advanced in vitro systems that closely mimic human physiology, such as organ-on-a-chip models like gut-liver-on-a-chip, can be crucial in improving drug efficacy while minimizing toxicity. Additionally, the adaptation of these technologies has the potential to significantly reduce both the time and cost associated with obtaining safe drug approvals, all while adhering to the 3Rs principle (replacement, reduction, refinement). In this review, we discuss the significance, current status, and future prospects of advanced platforms, specifically organ-on-a-chip models, in supporting preclinical drug discovery.
Insights
Advanced organ-on-a-chip models offer a promising solution to predict drug-induced liver injury (DILI). These systems improve drug efficacy and safety, reducing costs and time in drug development.
Area of Science:
- Biomedical Engineering
- Pharmacology
- Toxicology
Background:
- Drug development is lengthy and costly, with drug-induced liver injury (DILI) posing a significant challenge.
- Current preclinical models (animal and in vitro) poorly predict human DILI due to physiological differences.
- This leads to high failure rates in clinical trials and increased development costs.
Purpose of the Study:
- To review the significance, current status, and future prospects of advanced in vitro platforms for preclinical drug discovery.
- To highlight the potential of organ-on-a-chip (OOC) models in addressing DILI prediction challenges.
- To discuss how OOC technologies can accelerate drug approval while adhering to the 3Rs principles.
Main Methods:
- Review of current literature on organ-on-a-chip technologies in drug development.
- Focus on gut-liver-on-a-chip models as advanced in vitro systems.
- Discussion of the application of these platforms in assessing drug efficacy and toxicity.
Main Results:
- Organ-on-a-chip models, particularly gut-liver-on-a-chip systems, closely mimic human physiology.
- These advanced models show potential for improved prediction of DILI compared to traditional methods.
- Successful adaptation of OOC technology can enhance drug efficacy and minimize toxicity.
Conclusions:
- Organ-on-a-chip models are crucial for improving the accuracy of DILI risk assessment in preclinical drug discovery.
- These technologies offer a pathway to reduce drug development timelines and costs.
- OOC platforms support the 3Rs principles (replacement, reduction, refinement) in animal testing.
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