Related Experiment Video
Updated: May 24, 2025

Author Spotlight: Addressing Regulatory Gaps in Molecular Studies by Quantifying Viral Vectors in Complex Matrices
Published on: July 14, 2023
[Affordable gene therapies?]
1Biologiste, généticien et immunologiste, Président d'Aprogène (Association pour la promotion de la Génomique), 13007 Marseille, France.
Abstract:
Twenty gene therapies have now been approved in the USA by the FDA, but their stratospheric price tag (often above one million USD per patient) makes them essentially unaffordable for most. A systematic study of the various steps involved in the development and manufacture of these therapies, undertaken (among others) by the Innovative Genomics Institute in California, shows that the cost could be reduced up to tenfold without major legislative changes, and offers hope for affordable genetic therapies.
Related Concept Videos
Gene Therapy
X-linked Traits
What is Genetic Engineering?
iPS Cell Differentiation
CRISPR
The Central Dogma
RNA is the Missing Link Between DNA and Proteins
In the early 1900s, scientists discovered that DNA stores all the information needed for cellular functions and that proteins perform most of these functions. However, the mechanisms of converting genetic information into functional proteins remained unknown for many years. Initially, it was believed that a single gene is...

