Flow-cytometric MRD detection in pediatric T-ALL: a multicenter AIEOP-BFM consensus-based guided standardized

Michaela Reiterová1,2,3, Saskia Kohlscheen4, Oscar Maglia5

  • 1CLIP (Childhood Leukaemia Investigation Prague), Prague, Czech Republic.

Abstract

Insights

Standardized flow cytometry protocols effectively identify measurable residual disease (MRD) in T-acute lymphoblastic leukemia (T-ALL) patients, aiding risk stratification. This approach improves MRD detection for most T-ALL cases, though some require individualized analysis.

Area of Science:

  • Hematology
  • Immunology
  • Oncology

Background:

  • Measurable residual disease (MRD) monitoring is crucial for risk-based stratification in T-acute lymphoblastic leukemia (T-ALL).
  • T-ALL exhibits heterogeneity and rarity, often lacking standardized flow cytometry (FC)-based MRD measurement methods.
  • Poor treatment outcomes in relapsed T-ALL necessitate improved MRD detection and analysis.

Purpose of the Study:

  • To establish a standardized operating procedure (SOP) for T-ALL MRD detection using flow cytometry.
  • To develop and validate guided MRD gating strategies for T-ALL sample analysis.
  • To assess the applicability of standardized MRD panels and guided analysis in a large international study group.

Main Methods:

  • Consensus on markers and SOP for 8- and 12-color T-ALL MRD panels within the AIEOP-BFM-ALL-FLOW study group.
  • Testing of custom manufactured tubes with dried backbone antibodies against local FC standards.
  • Development of two guided MRD gating strategies for blast cell identification, compared to expert-based evaluation.

Main Results:

  • Analysis of 66 diagnostic and 67 day 15 samples using standardized MRD panels.
  • Optimized tubes correctly identified blast cells in all diagnostic samples.
  • Expert and guided MRD analysis of day 15 samples showed high correlation with local standards (Spearman R=0.98 and R=0.94, respectively).
  • Substantial discordance from local standards was minimal (3% for expert, 6% for guided analysis).

Conclusions:

  • Standardized operating procedures and guided analysis are effective for the majority of T-ALL MRD cases.
  • The developed approach demonstrates high applicability and correlation with existing standards.
  • Individualized analytical approaches may still be necessary for a subset of T-ALL cases due to challenging phenotypes.