Challenges in Assessing Response in Clinical Trials for Neurofibromatosis Type 1 Plexiform Neurofibromas

Eva Dombi¹, Andrea M Gross¹, Brigitte C Widemann¹+3

• ¹Eva Dombi, MD, Andrea M. Gross, MD, and Brigitte C. Widemann, MD, Pediatric Oncology Branch, Center for Cancer Research, National Cancer Institute, National Institutes of Health, Bethesda, MD; Brian D. Weiss, MD, Pediatric Hematology-Oncology, Riley Hospital for Children, Indiana University, Indianapolis, IN; Scott R. Plotkin, MD, PhD, Department of Neurology and Cancer Center, Massachusetts General Hospital, Boston, MA; and Shivani Ahlawat, MD, Russell H. Morgan Department of Radiology & Radiological Science, Johns Hopkins University School of Medicine, Baltimore, MD.