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Updated: May 21, 2025

Intrathecal Delivery of Antisense Oligonucleotides in the Rat Central Nervous System
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Recent advances in RNA-based therapeutics for neurodevelopmental disorders

Harini P Tirumala1, Huda Y Zoghbi2

  • 1Department of Human and Molecular Genetics, Baylor College of Medicine, Houston, TX 77030, USA; Jan and Dan Duncan Neurological Research Institute at Texas Children's Hospital, Houston, TX 77030, USA.

Current Opinion in Genetics & Development
|March 22, 2025
PubMed

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