Related Experiment Video

Updated: Jun 23, 2026

Multi-exon Skipping Using Cocktail Antisense Oligonucleotides in the Canine X-linked Muscular Dystrophy
10:30

Multi-exon Skipping Using Cocktail Antisense Oligonucleotides in the Canine X-linked Muscular Dystrophy

Published on: May 24, 2016

Antisense RNA therapies for muscular dystrophies

Virginia Arechavala-Gomeza1,2, Andrea López-Martínez1, Annemieke Aartsma-Rus3

  • 1Nucleic Acid Therapeutics for Rare Diseases (NAT-RD), Biobizkaia Health Research Institute, Barakaldo, Spain.

Journal of Neuromuscular Diseases
|March 28, 2025
PubMed

Keywords:
antisense oligonucleotidemuscle deliverymuscular dystrophysiRNA

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