Drug development for neglected ultra-rare diseases of no commercial interest: Challenges and opportunities

Related Experiment Video

Updated: Aug 4, 2026

ALS - Motor Neuron Disease: Mechanism and Development of New Therapies
15:48

ALS - Motor Neuron Disease: Mechanism and Development of New Therapies

Published on: July 29, 2007

Joseph A Katakowski1, Juan C López2

  • 1RTW Foundation, 40 Tenth Avenue, Third Floor, New York, NY 10014, USA.

Drug Discovery Today
|March 30, 2025
PubMed

Keywords:
patient advocacyphilanthropyultra-rare disease

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