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Gene Therapy

Gene Therapy

Gene therapy is a technique where a gene is inserted into a person’s cells to prevent or treat a serious disease. The added gene may be a healthy version of the gene that is mutated in the patient, or it could be a different gene that inactivates or compensates for the patient’s disease-causing gene. For example, in patients with severe combined immunodeficiency (SCID) due to a mutation in the gene for the enzyme adenosine deaminase, a functioning version of the gene can be...

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Encapsulated Cell Technology for the Delivery of Biologics to the Mouse Eye

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A new era for complement therapeutics

Trent M Woodruff¹

¹School of Biomedical Sciences, Health, Medicine and Behavioural Sciences, The University of Queensland, St Lucia, Brisbane, Australia.

The Journal of Allergy and Clinical Immunology

|April 12, 2025

Summary

No abstract available in PubMed .

Keywords:

C5aR1 Complement system anaphylatoxins autoimmunity disease eculizumab immunity inflammation membrane attack complex therapeutics

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