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Prenatal treatment of spinal muscular atrophy

Laurent Servais1

  • 1MDUK Oxford Neuromuscular Centre & NIHR Oxford Biomedical Research Centre, University of Oxford, Oxford, UK; Neuromuscular Reference Center, Department of Pediatrics, University Hospital Liège & University of Liège, Liège, Belgium.

Molecular Therapy : the Journal of the American Society of Gene Therapy
|April 19, 2025
PubMed
Abstract

No abstract available in PubMed .

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