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Draining the brain: Gene therapy reverses brain edema in mice with the leukodystrophy MLC

Rogier Min1, Niek P van Til1, Marjo S van der Knaap1

  • 1Department of Child Neurology, Amsterdam Leukodystrophy Center, Emma Children's Hospital, Amsterdam University Medical Center, Amsterdam Neuroscience, Amsterdam, the Netherlands; Department of Integrative Neurophysiology, Center for Neurogenomics and Cognitive Research, Vrije Universiteit Amsterdam, Amsterdam Neuroscience, Amsterdam, the Netherlands.

Molecular Therapy : the Journal of the American Society of Gene Therapy
|April 20, 2025
PubMed
Abstract

No abstract available in PubMed .

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