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The Ethics of Gene Therapy for Sickle Cell Disease

Amie Patel1, Alice Kuo1

  • 1Division of Medicine-Pediatrics, David Geffen School of Medicine, University of California Los Angeles, Los Angeles, USA.

Cureus
|April 23, 2025
PubMed

Keywords:
ethic considerationgene therapyinformed consentneurocognitive impairmentsickle cell disease: scd

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