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In utero genetic therapy: Treatment of early onset neurological disorders before they start

Beltran Borges1, Stephen M Brown2, Tippi C MacKenzie1

  • 1Department of Surgery, University of California, San Francisco, San Francisco, CA 94143, USA; UCSF Center for Maternal-Fetal Precision Medicine, San Francisco, CA 94158, USA; The Eli and Edythe Broad Center of Regeneration Medicine and Stem Cell Research, University of California, San Francisco, San Francisco, CA 94143, USA.

Molecular Therapy : the Journal of the American Society of Gene Therapy
|June 26, 2025
PubMed
Abstract

No abstract available in PubMed .

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