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Gene therapy for pediatric genetic kidney diseases

Yi Lu1,2, Yandong Song1, Shaokai Sun2

  • 1Key Laboratory of Immune Microenvironment and Disease (Ministry of Education) The Province and Ministry Co-sponsored Collaborative Innovation Center for Medical Epigenetics Department of Biochemistry and Molecular Biology School of Basic Medical Sciences Tianjin Institute of Urology The Second Hospital of Tianjin Medical University Tianjin Medical University Tianjin China.

Pediatric Discovery
|July 8, 2025
PubMed
Abstract

Keywords:
AAVAlport syndromeCRISPR‐Cas9LNPPKDgene therapypediatric genetic kidney diseases

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