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Forskolin-induced Swelling in Intestinal Organoids: An In Vitro Assay for Assessing Drug Response in Cystic Fibrosis Patients
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Impact of CFTR Modulators on Longitudinal Cystic Fibrosis Survival and Mortality: Review and Secondary Analysis

Jaime L Rubin1, Craig McKinnon2, Gabriel Ghizzi Pedra2

  • 1Vertex Pharmaceuticals Incorporated, 50 Northern Ave., Boston, MA, 02210, USA. jaime_rubin@vrtx.com.

Pulmonary Therapy
|July 11, 2025
PubMed
Abstract

Keywords:
Cystic fibrosisCystic fibrosis transmembrane conductance regulator modulatorsLung disease

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