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Generation of Human Nasal Epithelial Cell Spheroids for Individualized Cystic Fibrosis Transmembrane Conductance Regulator Study
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Cystinosis symposium: a rare disease model for comprehensive care

Ashley M Gefen1, Frederick J Kaskel2,3, Joshua J Zaritsky1

  • 1Division of Nephrology, Department of Pediatrics, Phoenix Children's Hospital, Phoenix, AZ, United States.

Frontiers in Pediatrics
|August 8, 2025
PubMed
Abstract

Keywords:
comprehensive carecystinosiscystinosis metabolic bone diseaserare diseasetransition

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