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Insights on Clinical Development of Cell and Gene Therapy for Rare Diseases-by DahShu Innovative Design Scientific

Chenkun Wang1, Junrui Di2, Mercedeh Ghadessi3

  • 1Vertex Pharmaceuticals, Inc., 50 Northern Avenue, Boston, MA, 02210, USA. Chenkun_Wang@vrtx.com.

Therapeutic Innovation & Regulatory Science
|August 8, 2025
PubMed

Keywords:
Cell and gene therapyClinical developmentRegulatory requirements and guidelinesSafety monitoring

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