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Advancing adeno-associated virus for Duchenne muscular dystrophy treatment: Moving beyond rodent models

Oluwatayo F Ikotun1,2, Elizabeth M McNally3, Melissa J Spencer2,4

  • 1Department of Medical and Molecular Pharmacology, David Geffen School of Medicine at UCLA, University of California, Los Angeles, Los Angeles, CA, USA.

Molecular Therapy. Methods & Clinical Development
|September 10, 2025
PubMed
Abstract

No abstract available in PubMed .

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