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Updated: Jan 14, 2026

Modeling Myotonic Dystrophy 1 in C2C12 Myoblast Cells
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Synthesis of Janus Bases for Targeting C‑G and U-U Pairs of CUG-RNA Repeats Associated with Myotonic Dystrophy Type 1

Shivaji A Thadke1, J Dinithi R Perera1, Savani W Thrikawala1

  • 1Department of Chemistry and Institute for Bimolecular Design and Discovery (IBD), Carnegie Mellon University, 4400 Fifth Avenue, Pittsburgh, Pennsylvania 15213, United States.

ACS Omega
|October 27, 2025
PubMed

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