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Targeting PAK1 or PAK4 Uncovers Different Mechanisms of Vascular Reprogramming in Pancreatic Cancer
Arian Ansardamavandi1, Chelsea Dumesny1, Sarah Ellis2,3
1Department of Surgery, Austin Precinct, The University of Melbourne, 145 Studley Rd, Melbourne, VIC 3084, Australia.
Abstract:
The tumour microenvironment in pancreatic ductal adenocarcinoma (PDA) regulates vascular function and therapeutic response. P21-activated kinases (PAKs) regulate cytoskeletal dynamics and angiogenesis; however, their roles in vascular reprogramming and chemotherapy responses remain unclear. This study examined the effects of a PAK1 knockdown (PAK1KD) and a PAK4 knockout (PAK4KO) on vascular remodelling in PDA. Human PANC-1 wild-type (WT), PAK1KD, and PAK4KO cells were injected subcutaneously into the flanks of SCID mice followed gemcitabine treatment. The tumour growth, vascular density, pericyte coverage, adhesion molecules, and hypoxia were determined. A proteomics study was used to identify the molecular changes involved in the vascular pathways. PAK1KD suppressed tumour growth and angiogenesis, promoted vascular normalisation, reduced hypoxia, and increased stromal ICAM-1. PAK4KO inhibited tumour growth, enlarged vessels, enhanced angiogenesis, and reduced hypoxia. PAK4KO did not affect adhesion molecules in the absence of gemcitabine, but markedly upregulated ICAM-1 and VCAM-1 with gemcitabine. Additionally, PAK4KO promoted vascular mimicry (VM) with a compromised integrity in tumour-derived vessels, but enhanced the integrity in endothelial-derived vessels. The proteomics study confirmed the enrichment of molecules in fibronectin and the VEGF pathway in PAK4KO cancer cells, along with the upregulation of EphA2, RhoA, ROCK1, ROCK2, and components of the EPH-ephrin signalling pathway, linking to enhanced VM. Neither PAK1KD nor PAK4KO increased the gemcitabine efficacy. In conclusion, PAK1KD and PAK4KO suppressed tumour growth with distinct vascular effects, but failed to enhance the gemcitabine responses, suggesting that PAK targeting reprograms the PDA vasculature, but offers limited benefit in chemotherapy-resistant models.
Insights
Targeting P21-activated kinases (PAKs) in pancreatic ductal adenocarcinoma suppressed tumor growth and altered tumor vasculature. However, neither PAK1 knockdown nor PAK4 knockout improved gemcitabine chemotherapy response in this model.
Area of Science:
- Oncology
- Molecular Biology
- Cancer Research
Background:
- The tumor microenvironment critically influences pancreatic ductal adenocarcinoma (PDA) vascular function and treatment outcomes.
- P21-activated kinases (PAKs) are implicated in cytoskeletal dynamics and angiogenesis, but their specific roles in PDA vascular reprogramming and chemotherapy response are not fully understood.
Purpose of the Study:
- To investigate the effects of PAK1 knockdown (PAK1KD) and PAK4 knockout (PAK4KO) on vascular remodeling and chemotherapy response in PDA.
- To elucidate the molecular mechanisms underlying vascular changes induced by PAK targeting in PDA.
Main Methods:
- Human PANC-1 wild-type, PAK1KD, and PAK4KO cells were xenografted into SCID mice and treated with gemcitabine.
- Tumor growth, vascular density, pericyte coverage, adhesion molecules, and hypoxia were assessed.
- Proteomics analysis was employed to identify molecular alterations in vascular pathways.
Main Results:
- PAK1KD suppressed tumor growth, angiogenesis, and hypoxia while promoting vascular normalization and increasing stromal ICAM-1.
- PAK4KO inhibited tumor growth, enhanced angiogenesis, and reduced hypoxia, but also enlarged vessels and promoted vascular mimicry (VM).
- PAK4KO upregulated adhesion molecules (ICAM-1, VCAM-1) with gemcitabine and revealed distinct effects on tumor-derived versus endothelial-derived vessel integrity. Proteomics identified enrichment in fibronectin and VEGF pathways, and upregulation of EphA2, RhoA, ROCK1/2, and EPH-ephrin signaling components, correlating with enhanced VM.
Conclusions:
- PAK1KD and PAK4KO exhibit distinct vascular effects and suppress tumor growth in PDA models.
- Neither PAK1KD nor PAK4KO enhanced gemcitabine efficacy, indicating that while PAK targeting reprograms PDA vasculature, it provides limited benefit in chemotherapy-resistant settings.
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