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AAV-mediated gene therapy for the CNS: The case for early treatment

Luanna E Liebscher Vidal1, Jose M Martinez-Navio1

  • 1Department of Pathology and Laboratory Medicine, Miller School of Medicine, University of Miami, Miami, FL, USA.

Molecular Therapy. Methods & Clinical Development
|December 11, 2025
PubMed
Abstract

No abstract available in PubMed .

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