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Effectiveness and safety of Risdiplam for types 1-3 spinal muscular atrophy in a single center

Xiaomei Zhu1, Hui Li2, Chaoping Hu1

  • 1Department of Neurology, Children`s Hospital of Fudan University, National Children`s Medical Center, Shanghai, China.

BMC Neurology
|December 26, 2025
PubMed
Abstract

No abstract available in PubMed .

Keywords:
EffectivenessMotor functionRisdiplamSafetySpinal muscular atrophy

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