Related Experiment Video

Updated: Jul 2, 2026

Systemic Delivery of MicroRNA Using Recombinant Adeno-associated Virus Serotype 9 to Treat Neuromuscular Diseases in Rodents
06:51

Systemic Delivery of MicroRNA Using Recombinant Adeno-associated Virus Serotype 9 to Treat Neuromuscular Diseases in Rodents

Published on: August 10, 2018

Meeting report: 2024 Muscular Dystrophy Association summit on 'Safety and challenges in gene therapy of neuromuscular

Angela Lek1, Evrim Atas1, Brian Lin1

  • 1Muscular Dystrophy Association, Chicago, IL, USA.

Journal of Neuromuscular Diseases
|January 19, 2026
PubMed

Keywords:
AAVgene therapymuscular dystrophyneuromuscular

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